First orphan drug for achondroplasia is validated
BioMarin Pharmaceutical Inc. recently announced that the European Medicines Agency [...]
ECRD2020 will take place online on 14-15 May
The Conference is a great opportunity to network and exchange invaluable knowledge with all stakeholders in the rare disease community
Postgraduate Course in Paediatric Bone and Mineral Metabolism
5 - 6th March 2020, Birmingham. Birmingham Children’s Hospital, a [...]
2019 call for membership to join ERNs
The call for healthcare providers to join the 24 existing [...]